{"id":4736,"date":"2019-06-02T21:04:34","date_gmt":"2019-06-02T18:04:34","guid":{"rendered":"https:\/\/mereusanatosi.ro\/wp\/?p=4736"},"modified":"2019-06-02T21:04:36","modified_gmt":"2019-06-02T18:04:36","slug":"medicamentul-experimental-care-trateaza-cea-mai-rara-boala-musculara-genetica","status":"publish","type":"post","link":"https:\/\/mereusanatosi.ro\/wp\/2019\/06\/02\/medicamentul-experimental-care-trateaza-cea-mai-rara-boala-musculara-genetica\/","title":{"rendered":"Medicamentul experimental care trateaz\u0103 cea mai rar\u0103 boal\u0103 muscular\u0103 genetic\u0103"},"content":{"rendered":"\n<figure class=\"wp-block-image\"><img loading=\"lazy\" width=\"800\" height=\"445\" src=\"https:\/\/mereusanatosi.ro\/wp\/wp-content\/uploads\/2019\/06\/boal\u0103-muscular\u0103-genetic\u0103-800x445.jpg\" alt=\"\" class=\"wp-image-4737\" srcset=\"https:\/\/mereusanatosi.ro\/wp\/wp-content\/uploads\/2019\/06\/boal\u0103-muscular\u0103-genetic\u0103-800x445.jpg 800w, https:\/\/mereusanatosi.ro\/wp\/wp-content\/uploads\/2019\/06\/boal\u0103-muscular\u0103-genetic\u0103-300x167.jpg 300w, https:\/\/mereusanatosi.ro\/wp\/wp-content\/uploads\/2019\/06\/boal\u0103-muscular\u0103-genetic\u0103-768x427.jpg 768w, https:\/\/mereusanatosi.ro\/wp\/wp-content\/uploads\/2019\/06\/boal\u0103-muscular\u0103-genetic\u0103.jpg 1067w\" sizes=\"(max-width: 800px) 100vw, 800px\" \/><figcaption>Surs\u0103 foto: http:\/\/www.newindianexpress.com<\/figcaption><\/figure>\n\n\n\n<p>Un nou studiu\narat\u0103 c\u0103 un medicament dezvoltat de cercet\u0103torii de la Indiana University pentru\na atenua simptomele unei boli musculo-scheletice rare este mult mai eficient dec\u00e2t\nterapiile conven\u021bionale. Hipofosfatemia legat\u0103 la X sau XLH este o boal\u0103 \u00een\ncare oragnismul pierde fosfatul, provoc\u00e2nd rahitism \u0219i alte afec\u021biuni\nmusculare. Aceast\u0103 boal\u0103 rar\u0103 genetic\u0103 afecteaz\u0103 aproximativ 1 din 20.000 de\npersoane. <\/p>\n\n\n\n<p>Cercet\u0103torii au recrutat\n61 de copii cu v\u00e2rste cuprinse \u00eentre 1 \u0219i 12 ani din 16 centre din \u00eentreag\u0103\nlume, inclusiv SUA, Canada, Marea Britanie, Suedia, Australia, Japonia \u0219i\nCoreea. Copiii au fost repartiza\u021bi la \u00eent\u00e2mplare, fie pentru a primi Burosumab,\nmedicamentul creat de crecet\u0103tori, fie pentru o injec\u021bie aprobat\u0103 de\nAdministra\u021bia pentru Alimente \u0219i Medicamente \u00een aprilie 2018, sau pentru\ntratamentele conven\u021bionale de administrare a fosfatului oral \u0219i a vitaminei D\nactive de mai multe ori pe zi. <\/p>\n\n\n\n<p>Copiii au fost observa\u021bi\ntimp de 64 de s\u0103pt\u0103m\u00e2ni, timp \u00een care cercet\u0103torii au descoperit c\u0103 72% dintre\ncopiii care au primit Burosumab au prezentat o vindecare substan\u021bial\u0103 a\nrahitismului, fa\u021b\u0103 de restul, care nu au avut rezultate at\u00e2t de bune. Acesta\neste primul studiu care a comparat Burosumab cu terapia conven\u021bional\u0103.\nMedicamentul blocheaz\u0103 o protein\u0103 numit\u0103 factor de cre\u0219tere fibroblast 23. &nbsp;<\/p>\n\n\n\n<p>Surs\u0103: https:\/\/www.sciencedaily.com<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Un nou studiu arat\u0103 c\u0103 un medicament dezvoltat de cercet\u0103torii de la Indiana University pentru a atenua simptomele unei boli<\/p>\n","protected":false},"author":1,"featured_media":4737,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":[],"categories":[101,177,64,11],"tags":[2398,2400,2401,2399],"_links":{"self":[{"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/posts\/4736"}],"collection":[{"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/comments?post=4736"}],"version-history":[{"count":1,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/posts\/4736\/revisions"}],"predecessor-version":[{"id":4738,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/posts\/4736\/revisions\/4738"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/media\/4737"}],"wp:attachment":[{"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/media?parent=4736"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/categories?post=4736"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/mereusanatosi.ro\/wp\/wp-json\/wp\/v2\/tags?post=4736"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}